DMD Guide for Families
Latest!
New 2018 DMD Guide for Families now available in US & UK.
Post marketing surveillance
Collection of safety and efficacy data once a drug has received conditional marketing approval
Publications
Latest publications!
Care guidelines for DMD & SMA - significant updates published
Industry
Download our industry brochure
Trial sites and patients, advisory support, study support, training
Disease information
Myotubular and centronuclear myopathy disease section now live!
IRDiRC recommends...
IRDiRC recommends our Patient Registries and also our Animal model SOPs
TACT
TREAT-NMD Advisory Committee for Therapeutics - application & review process, past reviews, committee etc
BioBanks
A unique network of biobanks storing quality DNA, cell & tissue samples on rare diseases and NMDs
Donate to TREAT-NMD
By supporting the work of the TREAT-NMD Alliance you can help us advance research
Advanced search
- Updated Standards of Care for Myotonic Dystrophy (DM1) Care standards are intended to help standardise and elevate care for the DM1 patient...
- TREAT-NMD Global Database Oversight Committee (TGDOC) Chair Elect - Expressions of Interest We must appoint a new TGDOC Chair Elect, and we would like to invite ...
- See Latest Newsletter
- Rare Disease Day 2019
28 Feb 2019 Rare Disease Day takes place on the last day of... - Orphan Drug Congress
17 -18 Jun 2019 With the accomplishment of preceding Rare Diseases Congress in 2018,... - See All Events
